Novel inhalable gene therapy trialed for people with cystic fibrosis
An inhalable medicine with the potential to improve lung disease in people with cystic fibrosis, irrespective of their ...
Gene Therapy Market to Hit USD 36.55 Billion by 2032 with 19.4% CAGR | MarketsandMarkets™.
The global Gene Therapy market, valued at US$7.21 billion in 2023, is forecasted to grow at a robust CAGR of 19.4%, reaching ...
Boehringer Ingelheim and partners start clinical development of a first-in-class, inhaled gene therapy for people with cystic fibrosis
Boehringer Ingelheim, IP Group, the UK Respiratory Gene Therapy Consortium (GTC)1 and OXB,1 today announce the start of LENTICLAIRTM 1, a Phase I/II trial of BI 3720931, a novel, first-in-class, gene ...
Medical training’s AI leap: How agentic RAG, open-weight LLMs and real-time case insights are shaping a new generation of doctors at NYU Langone
NYU Langone has built an LLM research companion and medical advisor, and is pioneering what it calls AI-driven “precision medical education." ...
ophthalmologytimes1d
Shaping the future of retinal therapy
The introduction of anti-VEGF agents has revolutionized the field of medical retina care by reducing rates of vision loss and ...
Scientists Uncover a Tiny Gene That Could End Dangerous Heart Arrhythmias
Researchers have identified a gene therapy that could prevent life-threatening arrhythmias by restoring the heart’s ...
TMCnet15h
EG 427 raises €27 million in successful Series B co-led by Andera Partners and Bpifrance to finance on-going clinical study and platform development
Paris, France, February 20, 2025 – EG 427, a biotechnology company leading the development of pinpoint genetic medicines for prevalent chronic diseases in neurology, announced today the successful ...
4D Molecular Therapeutics: A Smart Bet On Long-Term VEGF Suppression
D Molecular Therapeutics is undervalued, with its lead candidate 4D-150 showing potential. Click here to find out why I rate ...
What a $2 million per dose gene therapy reveals about drug pricing
Vincent Gaynor remembers, almost to the minute, when he realized his part in birthing the breakthrough gene therapy Zolgensma ...