Researchers from the NIHR Moorfields Biomedical Research Centre and University College London have found that gene therapy improved visual acuity and preserved retinal structure in young children with ...
MeiraGTx’s investigational gene therapy AAV-AIPL1 has improved the sight of 11 children who were born blind. MeiraGTx is ...
A single injection of a healthy gene allowed blind children to recognize objects, shapes, and even read — offering hope for ...
The vision of one child with AIPL1-associated severe retinal dystrophy improved from light perception to naming his favourite ...
The AAV-AIPL1 therapy is designed to address severe sight impairment caused by mutations in the AIPL1 gene. This condition is a form of retinal dystrophy that leads to severe visual impairment ...
"We have, for the first time, an effective treatment for the most severe form of childhood blindness, and a potential ...
Toddlers who were born with the most severe form of childhood blindness can now see after groundbreaking gene therapy ...
The children were born with a severe impairment to their sight due to a rare genetic deficiency that affects the AIPL1 gene ... show that gene therapy at an early age can dramatically improve ...
Toddlers who were born with the most severe form of childhood blindness can now see after groundbreaking gene therapy treatment ... deficiency that affects the AIPL1 gene.