Scientists in the UK have successfully used gene therapy to restore some vision to legally blind children with an inherited retinal condition. All 11 children in the clinical trial saw improvements ...

A new study led by Profs. Fan Kelong and Yan Xiyun from the Institute of Biophysics of the Chinese Academy of Sciences ...

A study led by UMass Chan Medical School researchers has demonstrated that a gene therapy to correct a mutation that causes ...

A single injection of a healthy gene allowed blind children to recognize objects, shapes, and even read — offering hope for ...

The vision of one child with AIPL1-associated severe retinal dystrophy improved from light perception to naming his favourite ...

A gene therapy treatment has enabled sight improvements for blind infants, through pioneering work by University College ...

Researchers from the NIHR Moorfields Biomedical Research Centre and University College London have found that gene therapy improved visual acuity and preserved retinal structure in young children with ...

The biotech has met with UK regulators to discuss a marketing authorization application under exceptional circumstances based on data from 11 patients.

"We have, for the first time, an effective treatment for the most severe form of childhood blindness, and a potential ...

In a major breakthrough, four children born with severe visual impairments have experienced life-changing improvements in their ...

Four young children have gained life-changing improvements in sight following treatment with a pioneering new genetic ...

MeiraGTx’s investigational gene therapy AAV-AIPL1 has improved the sight of 11 children who were born blind. MeiraGTx is ...