Agios Pharmaceuticals is discontinuing development of its oral therapy candidate, tebapivat, for people with sickle cell disease (SCD). The decision follows results from a small Phase 2 clinical trial ...
Columnist Oluwatosin Adesoye highlights a discrepancy between medical literature and patient experiences regarding ...
For a condition that affects millions worldwide, treatment progress for sickle cell disease (SCD) has been slow. In the United States alone, an estimated 100,000 people are living with the disease, ...
The U.S. Food and Drug Administration (FDA) has granted priority review — a decision that could speed a drug’s approval — to an application for the oral therapy mitapivat for sickle cell disease (SCD) ...
Casgevy (exagamglogene autotemcel) is now approved in the U.S. to treat children as young as 2 with sickle cell disease (SCD) and recurrent vaso-occlusive crises (VOCs). The U.S. Food and Drug ...
A low dose of Vascarta‘s VAS-101, a curcumin-based gel being developed for sickle cell disease (SCD), was well tolerated and showed early signs of reducing red blood cell sickling, pain, and fatigue ...
Share this page with email Share this page on Facebook Share this page on X Share this page on Reddit Print Preferred Source on Google Children with sickle cell anemia, the most common and severe form ...
Agios Pharmaceuticals’ medication mitapivat rapidly increased levels of the oxygen-carrying protein hemoglobin in patients ages 16 and older with sickle cell disease (SCD), while also being linked to ...
An experimental, single-dose gene-editing therapy from Tessera Therapeutics successfully corrected the genetic mutation that causes sickle cell disease (SCD) in the majority of blood-forming stem ...
Beam Therapeutics plans to ask the U.S. Food and Drug Administration (FDA) to approve ristoglogene autogetemcel, or risto-cel, its single-dose, gene-edited cell therapy candidate for people with ...
Through a project aimed at building empathy and understanding among clinicians about sickle cell disease (SCD)-related pain episodes, a team of nurses in Chicago has helped standardize emergency care ...
A sickle cell crisis isn’t a polite guest, and it often arrives unannounced. Over the years, I’ve learned that my crises either come on suddenly or build gradually, with subtle clues or a red alert.
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